CRISPR Therapeutics recently reported that rollout of its approved gene therapy Casgevy for sickle cell disease and transfusion‑dependent beta thalassemia has been slower than hoped, contributing to a ...

Gene editing, a set of techniques used to alter sections of an organism's DNA, is helping scientists cure diseases previously ...

编辑丨王多鱼排版丨水成文CRISPR-Cas9 基因编辑技术为遗传疾病的治疗带来革命性突破，FDA 已批准了基于 CRISPR-Cas9 的基因编辑疗法 Casgevy 用于治疗镰状细胞病（SCD）和 β-地中海贫血（TDT）。之前对于其安全性的研究，通常聚焦于脱靶效应引发的基因组序列改变，往往忽视了其对细胞表观基因组及其功能的影响。2026 年 ...

One year after receiving CRISPR gene editing therapy at CHOP, a Delaware County baby is thriving, and doctors want to expand ...

Rapid advancements in CRISPR and next-generation gene editing technologies, combined with a strong clinical pipeline ...

A research group led by Associate Professor Tetsuya Muramoto from the Faculty of Science, Toho University, has established a ...

For years, researchers have been trying to figure out how to treat inherited blood disorders like sickle cell disease without causing new health problems in the process. Now, a team of scientists from ...

CRISPR isn't profitable, but it does have an approved gene therapy treatment with loads of potential.

CRISPR gene drives bias inheritance in pests, advancing population-level control while raising questions about resistance and ...

Revvity's Dharmacon All-in-one lentiviral platform has expanded to include whole-genome library options for CRISPR knockout (CRISPRko), CRISPR interference (CRISPRi), and CRISPR activation (CRISPRa).